TY  - GEN 
AU  - De Castro López, María José
AU  - Del Toro, M.
AU  - Giugliani, R.
AU  - Couce Pico, María Luz
PY  - 2021
SN  - 1661-6596
UR  - http://hdl.handle.net/20.500.11940/17393
AB  - The need for long-lasting and transformative therapies for mucopolysaccharidoses (MPS) cannot be understated. Currently, many forms of MPS lack a specific treatment and in other cases available therapies, such as enzyme replacement therapy (ERT), do...
LA  - en
TI  - Gene Therapy for Neuronopathic Mucopolysaccharidoses: State of the Art
DO  - 10.3390/ijms22179200
VL  - 22
ER  -