TY  - JOUR 
AU  - Ortolano, S.
AU  - Vieitez, I.
AU  - Navarro, C.
AU  - Spuch, C.
PY  - 2014
SN  - 1872-2148
UR  - http://hdl.handle.net/20.500.11940/5752
AB  - Lysosomal storage diseases (LSDs) are a group of rare genetic multisystemic disorders, resulting in deficient lysosomal activity. These pathologies are characterized by progressive accumulation of storage material within the lysosomes, ultimately...
LA  - eng
KW  - Cell- and Tissue-Based Therapy
KW  - Drug Delivery Systems
KW  - Enzyme Inhibitors
KW  - Enzyme Replacement Therapy
KW  - Genetic Therapy
KW  - Humans
KW  - Lysosomal Storage Diseases
KW  - Models, Biological
KW  - Molecular Chaperones
KW  - Patents as Topic
TI  - Treatment of lysosomal storage diseases: recent patents and future strategies
DO  - 10.2174/1872214808666140115111350
T2  - Recent patents on endocrine, metabolic & immune drug discovery.
M2  - 9
VL  - 8
ER  -